Condition: Dilated Cardiomyopathy (DCM) · Sponsor: Rocket Pharmaceuticals Inc.
Sponsor, CRO or site team? See where this study is running → — listed sites, countries and recruiting context. Everything below is written for patients and caregivers.
This is a Phase 1, open-label, dose-escalation trial to characterize the safety, tolerability, and preliminary efficacy of RP-A701 following a single IV administration in high-risk adult patients with BAG3-DCM.
This description comes directly from the study's public registry record.
Clinical Information · 646-627-0033 · clinicaltrials@rocketpharma.com
Always discuss trial participation with your own doctor first.
| University of California, San Diego | San Diego, California, United States | Recruiting |
| Mayo Clinic | Rochester, Minnesota, United States | Recruiting |
| Medical University of South Carolina | Charleston, South Carolina, United States | Recruiting |
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