Recruiting studies: Neuronal Ceroid Lipofuscinosis

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

Assessment of Pressure Pain Threshold (PPT) and Conditioned Pain Modulation (CPM) After Effect in Patients With and With
NA · 1 location(s) · The Hashemite University · NCT07178288 Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Database
Phase N/A · 1 location(s) · Universitätsklinikum Hamburg-Eppendorf · NCT04613089 UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Phase 1 · 1 location(s) · Joanne Kurtzberg, MD · NCT02254863 Clinical and Neuropsychological Investigations in Batten Disease
Phase N/A · 1 location(s) · University of Rochester · NCT01873924 Italian NCL Registry: a Registry for NCL as an Integration Tool for Future Therapeutic Strategies
Phase N/A · 1 location(s) · IRCCS Fondazione Stella Maris · NCT06844877 Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Phase N/A · 2 location(s) · Sanford Health · NCT01793168 A First-in-Human, Open-Label, Dose-Escalation Study to Evaluate the Safety and Tolerability of Gene Therapy With TTX-381
Phase 1/Phase 2 · 2 location(s) · Tern Therapeutics, LLC · NCT05791864 Investigations of Juvenile Neuronal Ceroid Lipofuscinosis
Phase N/A · 1 location(s) · Eunice Kennedy Shriver National Institute of Child Health an · NCT03307304 Caregiving Networks Across Disease Context and the Life Course
Phase N/A · 1 location(s) · National Human Genome Research Institute (NHGRI) · NCT05007990 NYSCF Scientific Discovery Biobank
Phase N/A · 1 location(s) · New York Stem Cell Foundation Research Institute · NCT06203106 Longitudinal Study of Neurodegenerative Disorders
Phase N/A · 1 location(s) · University of Pittsburgh · NCT03333200 Inherited Retinal Degenerative Disease Registry
Phase N/A · 1 location(s) · Foundation Fighting Blindness · NCT02435940

Look up another condition

Patient organization or foundation? You can brand this page for your community — your logo, your resources, same honest registry data, kept current daily. Ask about branding →

This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.