Condition: MLD · Krabbe Disease · ALD · Sponsor: University of Pittsburgh
The purpose of this study is to understand the course of rare genetic disorders that affect the brain. This data is being analyzed to gain a better understanding of the progression of the rare neurodegenerative disorders and the effects of interventions.
This description comes directly from the study's public registry record.
Deepa Rajan, MD · 412-692-8388 · rajands@upmc.edu
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| UPMC Children's Hospital of Pittsburgh | Pittsburgh, Pennsylvania, United States | Recruiting |
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Source record: clinicaltrials.gov/study/NCT03333200