EICHOR

Recruiting studies: Spinal Muscle Atrophy

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene After a Single Intravenous Ad
Phase 1/Phase 2 · 7 location(s) · Biocad · NCT05747261 A Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With Zolgensma
Phase N/A · 2 location(s) · Novartis Pharmaceuticals · NCT06019637 Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Phase N/A · 2 location(s) · Sanford Health · NCT01793168 A Study of Risdiplam in Participants With Type I and Type II Spinal Muscle Atrophy (SMA)
Phase N/A · 2 location(s) · Hoffmann-La Roche · NCT07531719 Long Read Analysis in Spinal Muscular Atrophy - LOREASI
NA · 1 location(s) · University Hospital, Rouen · NCT07332702 Bicalutamide and Abemaciclib in Inoperable or Metastatic Androgen Receptor-positive Triple-negative Breast Cancer
Phase 2 · 6 location(s) · Universitaire Ziekenhuizen KU Leuven · NCT06365788 TulmiSTAR-02: A Phase I/II Open-label Study of Tulmimetostat in Combination With Darolutamide vs. Darolutamide, and Tulm
Phase 1/Phase 2 · 31 location(s) · Novartis Pharmaceuticals · NCT07190300 A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pe
Phase 1 · 19 location(s) · Biogen · NCT06555419 Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular D
NA · 1 location(s) · Institut de Myologie, France · NCT07321977 Clinical Procedures to Support Research in ALS
Phase N/A · 11 location(s) · University of Miami · NCT03489278 Neonatal Spinal Muscular Atrophy (SMA) Screening
Phase N/A · 1 location(s) · Kaohsiung Medical University Chung-Ho Memorial Hospital · NCT03217578 Development of IPS from Donated Somatic Cells of Patients with Neurological Diseases
Phase N/A · 1 location(s) · Hadassah Medical Organization · NCT00874783 Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients
Phase 1/Phase 2 · 1 location(s) · GeneCradle Inc · NCT06421831 Toward Ubiquitous Lower Limb Exoskeleton Use in Children and Young Adults
Phase N/A · 1 location(s) · National Institutes of Health Clinical Center (CC) · NCT06998134 A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Phase 2 · 25 location(s) · Scholar Rock, Inc. · NCT07047144 Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
Phase N/A · 1 location(s) · Assistance Publique - Hôpitaux de Paris · NCT06147414 Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia
NA · 2 location(s) · Leigh R. Hochberg, MD, PhD. · NCT05724173 Nomad P-KAFO Study
NA · 1 location(s) · Shirley Ryan AbilityLab · NCT05644522 Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
NA · 21 location(s) · Alcyone Therapeutics, Inc · NCT05866419 Natural History of SMA
Phase N/A · 5 location(s) · Fondazione Policlinico Universitario Agostino Gemelli IRCCS · NCT05755451 A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atr
Phase 4 · 19 location(s) · Hoffmann-La Roche · NCT05861999 A Registered Cohort Study on SMA
Phase N/A · 1 location(s) · Wan-Jin Chen · NCT04010604 Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular A
Phase N/A · 1 location(s) · St. Jude Children's Research Hospital · NCT06532474 Effects of Whole-body Electrical Muscle Stimulation Exercise on Spinal Motoneuronal Activation in Older Adults
NA · 1 location(s) · University of Missouri-Columbia · NCT06689618 The Effect of a Muscle-mimicking, Fabric-type Shoulder Orthosis on Functional Movements of the Upper Limb in Patients Wi
NA · 1 location(s) · Seoul National University Hospital · NCT06363357 Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1
Phase 1/Phase 2 · 1 location(s) · Gemma Biotherapeutics · NCT07070999 BrainGate2: Feasibility Study of an Intracortical Neural Interface System for Persons With Tetraplegia
NA · 6 location(s) · Leigh R. Hochberg, MD, PhD. · NCT00912041 Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Musc
NA · 1 location(s) · Centre Hospitalier Universitaire de Liege · NCT07286565 A Registry Based Randomized-Controlled Trial of an Upper Limb Exergaming Intervention for Children and Adolescents With
NA · 5 location(s) · Maryam Oskoui, MD, MSc, FRCPC, FAAN · NCT06396325 Clinical, Molecular and Imaging Biomarkers in Spinal and Bulbar Muscular Atrophy (SBMA)
Phase N/A · 1 location(s) · National Institute of Neurological Disorders and Stroke (NIN · NCT04944940

Look up another condition

Patient organization or foundation? You can brand this page for your community — your logo, your resources, same honest registry data, kept current daily. Ask about branding →