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A Study of Risdiplam in Participants With Type I and Type II Spinal Muscle Atrophy (SMA)
Condition: Spinal Muscle Atrophy · Sponsor: Hoffmann-La Roche
About this study
This multicenter, non-interventional, prospective study with a retrospective component aims to evaluate the real-world clinical outcomes, safety profile, and motor function improvements of Risdiplam treatment in participants with Type I and Type II Spinal Muscle Atrophy over 24 months of treatment. The study will allow retrospective collection of medical history data and previous participants visits from the medical records.
This description comes directly from the study's public registry record.
Talk to the study team
Reference Study ID Number: ML45655 https://forpatients.roche.com/ No attachments to email below. · 888-662-6728 (U.S. Only) · global-roche-genentech-trials@gene.com
Fastest response: use the inquiry form. https://www.gene.com/contact-us/submit-medical-inquiry
Always discuss trial participation with your own doctor first.
Locations (2)
| Neurology Department, Ain Shams University Hospitals | Cairo, Egypt | Recruiting |
| Air Force Specialized Hospital | Cairo, Egypt | Recruiting |
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Source record: clinicaltrials.gov/study/NCT07531719