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Condition: Sma Spinal Muscular Atrophy Synced from ClinicalTrials.gov · July 29, 2026

Recruiting studies: Sma Spinal Muscular Atrophy

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

Clinical Trial of Mexiletine Hydrochloride for Spinal and Bulbar Muscular Atrophy
Phase 2/Phase 3 · 5 location(s) · Masahisa Katsuno · NCT06862596A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or
Phase N/A · 14 location(s) · Biogen · NCT05789758Observational Study to Observe Variations of Gait Parameters in Patients With Neuromuscular Diseases
Phase N/A · 2 location(s) · IRCCS Eugenio Medea · NCT06666816Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Typ
Phase 3 · 7 location(s) · GeneCradle Inc · NCT06971094French Register of Patients With Spinal Muscular Atrophy
Phase N/A · 1 location(s) · Assistance Publique - Hôpitaux de Paris · NCT04177134Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatments
Phase N/A · 5 location(s) · Fondazione Policlinico Universitario Agostino Gemelli IRCCS · NCT05768048Assessing the Fertility Status of Men With Spinal Muscular Atrophy (SMA)
Phase N/A · 1 location(s) · Bar-Chama, Natan, M.D. · NCT06194539Impairments of Neuro-muscular Communication in Motor-Neuron Disease: A Bio-Marker for Early and Personalised Diagnosis
Phase N/A · 1 location(s) · University of Dublin, Trinity College · NCT05663008Characterization of New Phenotypes of Patients With Spinal Muscular Atrophy Treated With SMN Restoring Therapy
NA · 8 location(s) · Hospices Civils de Lyon · NCT06321965A Trial to Learn How Safe AZD9750 is and How Well it Works in People With Metastatic Prostate Cancer When Given With or
Phase 1/Phase 2 · 18 location(s) · AstraZeneca · NCT07336446A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atr
Phase 4 · 19 location(s) · Hoffmann-La Roche · NCT05861999A Study to Compare the Efficacy and Safety of BMS-986365 Versus the Investigator's Choice of Therapy in Participants Wit
Phase 3 · 281 location(s) · Celgene · NCT06764485A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration
Phase 2 · 17 location(s) · argenx · NCT07287982HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
NA · 1 location(s) · Teachers College, Columbia University · NCT07488338Real World Clinical Effectiveness & Safety of Vesemnogene Lantuparvovec for Spinal Muscular Atrophy (SMA) in Low-middle
Phase 3 · 1 location(s) · Lantu Biopharma · NCT07265232A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pe
Phase 1 · 19 location(s) · Biogen · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
NA · 21 location(s) · Alcyone Therapeutics, Inc · NCT05866419Clinical, Molecular and Imaging Biomarkers in Spinal and Bulbar Muscular Atrophy (SBMA)
Phase N/A · 1 location(s) · National Institute of Neurological Disorders and Stroke (NIN · NCT04944940Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Musc
NA · 1 location(s) · Centre Hospitalier Universitaire de Liege · NCT07286565Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
Phase N/A · 1 location(s) · Assistance Publique - Hôpitaux de Paris · NCT06147414Neonatal Spinal Muscular Atrophy (SMA) Screening
Phase N/A · 1 location(s) · Kaohsiung Medical University Chung-Ho Memorial Hospital · NCT03217578Long Read Analysis in Spinal Muscular Atrophy - LOREASI
NA · 1 location(s) · University Hospital, Rouen · NCT07332702A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Particip
Phase 4 · 16 location(s) · Hoffmann-La Roche · NCT05861986Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
Phase N/A · 1 location(s) · Columbia University · NCT06955897Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar
Phase N/A · 1 location(s) · Medstar Health Research Institute · NCT07223489Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients
Phase 1/Phase 2 · 1 location(s) · GeneCradle Inc · NCT06421831Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)
NA · 1 location(s) · Johns Hopkins University · NCT07521930Test of Aquatic Mobility of SMA Infants
NA · 1 location(s) · Assistance Publique - Hôpitaux de Paris · NCT06152302Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular A
Phase N/A · 1 location(s) · St. Jude Children's Research Hospital · NCT06532474A Head-to-head Study Comparing the Functional Value of Two Models of Robotically Assisted Rehabilitation in SMA (Spinal
NA · 1 location(s) · Wiktor Dega University Orthopedic and Rehabilitation Hospita · NCT06322654
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This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.