Condition: Spinal Muscular Atrophy · Sponsor: Hospices Civils de Lyon
With the advent of new treatments for ASI, new phenotypes are emerging. The investigators propose to describe these new phenotypes by prospectively following children with ASI of all types treated with TRS and aged under 16 for 2 years. The investigators also propose to evaluate potential assessment tools to determine whether they are relevant for monitoring this population, either routinely or for future clinical trials. The investigators also aim to collect the total costs associated with ASI in order to propose a first prospective medico-economic study in France.
This description comes directly from the study's public registry record.
Laure LE GOFF, PI · 04.72.12.95.04 · laure.le-goff@chu-lyon.fr
Tiphanie GINHOUX · 04.27.85.77.23 · Tiphanie.ginhoux01@chu-lyon.fr
Always discuss trial participation with your own doctor first.
| Pediatric Rehabilitation Service - L'Escale Mother and Child Hospital | Bron, Rhone, France | Recruiting |
| CHRU of Brest | Brest, France | Not Yet Recruiting |
| Pediatric Neurology and Resuscitation Raymond-Poincare Hospital | Garche, France | Not Yet Recruiting |
| Pediatric Neurology Swynghedauw Hospital | Lille, France | Not Yet Recruiting |
| Marseille University Hospital - Timone Hospital Department of Pediatric Neurology - Specialized Pediatrics and Child Medicine | Marseille, France | Not Yet Recruiting |
| I-Motion Pediatric Clinical Trial Platform Armand Trousseau Hospital | Paris, France | Not Yet Recruiting |
| Hautepierre Hospital - Mother and Child Hospital | Strasbourg, France | Not Yet Recruiting |
| Department of Pediatrics - Neurology and Infectious Diseases Toulouse University Hospital - Children's Hospital | Toulouse, France | Not Yet Recruiting |
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Source record: clinicaltrials.gov/study/NCT06321965