Recruiting studies: Rett Syndrome

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administer
Phase 1/Phase 2 · 11 location(s) · Ionis Pharmaceuticals, Inc. · NCT06430385 Measuring Impact of Computer Gaming on Arm Use in Rett Syndrome
NA · 1 location(s) · Georgetown University · NCT05012475 Repurposing Mirtazapine in Rett Syndrome
Phase 2 · 4 location(s) · University of Trieste · NCT07430046 Rett REVOLUTION Trial: An Exploratory Evaluation of the Safety and Efficacy of Vorinostat in Rett Syndrome
Phase 1 · 1 location(s) · Unravel Biosciences, Inc. · NCT07150013 Auditory EEG and Behavioral Assessments in Individuals With Rett Syndrome
Phase N/A · 1 location(s) · University of Rochester · NCT07569445 Cognitive Function in Rett Syndrome During Trofinetide Treatment
Phase N/A · 1 location(s) · University of Minnesota · NCT06705816 Neurophysiologic Biomarkers in Rett Syndrome
Phase N/A · 6 location(s) · Children's Hospital of Philadelphia · NCT05932589 Safety and Preliminary Efficacy of TSHA-102 Gene Therapy in Pediatric Females Aged >2 to <4 Years With Rett Syndrome
Phase 3 · 1 location(s) · Taysha Gene Therapies, Inc. · NCT07480564 To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
Phase 3 · 18 location(s) · Biomed Industries, Inc. · NCT06840496 The Rett Syndrome Global Registry
Phase N/A · 1 location(s) · Rett Syndrome Research Trust · NCT04900493 Rett Syndrome Registry
Phase N/A · 19 location(s) · International Rett Syndrome Foundation · NCT05432349 GROWing Up With Rare GENEtic Syndromes
Phase N/A · 1 location(s) · dr. Laura C. G. de Graaff-Herder · NCT04463316 Intensive Multimodal Neurorehabilitation Targeting Neuroplasticity in Pediatric Neurodevelopmental and Chromosomal Disor
Phase N/A · 1 location(s) · Healing Hope International · NCT07493096 Validating Innovative Biosensors for Rett Autonomic Symptom Tracking
Phase N/A · 3 location(s) · Rett Syndrome Research Trust · NCT06338267 Gene Editing as a Therapeutic Approach for Rett Syndrome
Phase N/A · 1 location(s) · University of Siena · NCT05740761

Look up another condition

Patient organization or foundation? You can brand this page for your community — your logo, your resources, same honest registry data, kept current daily. Ask about branding →

This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.