Recruiting studies: Pompe Disease Late Onset

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Phase 2 · 28 location(s) · Shionogi · NCT07123155 Pompe Disease Registry Protocol
Phase N/A · 272 location(s) · Genzyme, a Sanofi Company · NCT00231400 Long-Term Development of Muscular Dystrophy Outcome Assessments
Phase N/A · 1 location(s) · Virginia Commonwealth University · NCT05989620 Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug
Phase 1/Phase 2 · 1 location(s) · GeneCradle Inc · NCT06391736 A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Lat
Phase 1/Phase 2 · 9 location(s) · AskBio Inc · NCT07282847 Pompe Pregnancy Sub-Registry
Phase N/A · 35 location(s) · Genzyme, a Sanofi Company · NCT00567073 A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset P
Phase 1 · 3 location(s) · Denali Therapeutics Inc. · NCT07354724 Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
NA · 1 location(s) · University of Missouri-Columbia · NCT07478172

Look up another condition

Patient organization or foundation? You can brand this page for your community — your logo, your resources, same honest registry data, kept current daily. Ask about branding →

This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.