● Recruiting

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Condition: Pompe Disease · Sponsor: Shionogi

PhasePhase 2

Planned participants45

Who can joinAll sexes, 18 Years to no upper limit

Healthy volunteersNo

About this study

The purpose of this study is to evaluate the safety, pharmacodynamics (PD), and exploratory clinical efficacy of S-606001 in adult participants with LOPD as an add-on to ERT.

This description comes directly from the study's public registry record.

Talk to the study team

Shionogi Clinical Trials Administrator Clinical Support Help Line · 800-849-9707 · Shionogiclintrials-admin@shionogi.co.jp

Always discuss trial participation with your own doctor first.

Locations (28)

University of California - Irvine Medical Center	Irvine, California, United States	Recruiting
University of Florida (UF) - Gainesville	Gainesville, Florida, United States	Recruiting
Emory University Hospital	Atlanta, Georgia, United States	Recruiting
Washington University in St. Louis	St Louis, Missouri, United States	Recruiting
Duke University Medical Center	Durham, North Carolina, United States	Recruiting
Cincinnati Children's Hospital Medical Center	Cincinnati, Ohio, United States	Recruiting
University of Pennsylvania	Philadelphia, Pennsylvania, United States	Recruiting
University of Pittsburgh School of Medicine	Pittsburgh, Pennsylvania, United States	Recruiting
Lysosomal and Rare Disorders Research and Treatment Center (LDRTC)	Fairfax, Virginia, United States	Recruiting
UZ Leuven	Leuven, Belgium	Recruiting
Aarhus University Hospital	Aarhus, Denmark	Recruiting
HLC Hopital Pierre Wertheimer	Bron, France	Recruiting

+ 16 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT07123155