Condition: Glycogen Storage Disease Type II (GSD-II) · Pompe Disease (Late-onset) · Glycogenesis 2 Acid Maltase Deficiency · Sponsor: Genzyme, a Sanofi Company
This Sub-registry is a multicenter, international, longitudinal, observational, and voluntary program designed to track pregnancy outcomes for any pregnant woman enrolled in the Pompe Registry, regardless of whether she is receiving disease-specific therapy (such as ERT with alglucosidase alfa or avalglucosidase alfa) and irrespective of the commercial product with which she may be treated. No experimental intervention is given; thus a patient will undergo clinical assessments and receive standard of care treatment as determined by the patient's physician. The primary objective of this Sub-registry is to track pregnancy outcomes, including complications and infant growth, in all women with Pompe disease during pregnancy, regardless of whether they receive disease-specific therapy, such as ERT with alglucosidase alfa or avalglucosidase alfa.
This description comes directly from the study's public registry record.
Trial Transparency email recommended (Toll free number for US & Canada) · 800-633-1610 · Contact-us@sanofi.com
Pompe Registry HelpLine · 617-591-5500
Always discuss trial participation with your own doctor first.
| Barrow Neurol Group- Site Number : 840087 | Phoenix, Arizona, United States | Recruiting |
| University of Florida Pediatrics Genetics- Site Number : 157138 | Jacksonville, Florida, United States | Recruiting |
| Emory University School Of Medicine- Site Number : 840060 | Atlanta, Georgia, United States | Recruiting |
| Indianapolis University School of Medicine- Site Number : 840027 | Indianapolis, Indiana, United States | Recruiting |
| University of Iowa- Site Number : 150294 | Iowa City, Iowa, United States | Recruiting |
| Spectrum for Health- Site Number : 840019 | Grand Rapids, Michigan, United States | Recruiting |
| Washington University- Site Number : 150612 | St Louis, Missouri, United States | Recruiting |
| New York University School Of Medicine- Site Number : 840040 | New York, New York, United States | Recruiting |
| Mt. Sinai School of Medicine- Site Number : 840005 | New York, New York, United States | Recruiting |
| Columbia University Irving Medical Center- Site Number : 157199 | New York, New York, United States | Recruiting |
| Duke University Medical Center Genetics Dept- Site Number : 840037 | Durham, North Carolina, United States | Recruiting |
| LSD Data Registry Site LLC- Site Number : 840094 | Dublin, Ohio, United States | Recruiting |
+ 23 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT00567073