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Condition: Mucopolysaccharidosis Ii Synced from ClinicalTrials.gov · July 28, 2026

Recruiting studies: Mucopolysaccharidosis Ii

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB
Phase 1/Phase 2 · 3 location(s) · JCR Pharmaceuticals Co., Ltd. · NCT06488924Registry of Patients Diagnosed With Lysosomal Storage Diseases
Phase N/A · 1 location(s) · University of California, San Francisco · NCT05619900UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Phase 1 · 1 location(s) · Joanne Kurtzberg, MD · NCT02254863A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II
Phase 2/Phase 3 · 5 location(s) · AO GENERIUM · NCT05208281MPS (RaDiCo Cohort) (RaDiCo-MPS)
Phase N/A · 23 location(s) · Institut National de la Santé Et de la Recherche Médicale, F · NCT06036693PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Phase 1 · 1 location(s) · University of California, San Francisco · NCT04532047Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Phase N/A · 1 location(s) · Paul Szabolcs · NCT04528355Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH
Phase 2/Phase 3 · 5 location(s) · Ultragenyx Pharmaceutical Inc · NCT02716246A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult P
Phase 2/Phase 3 · 32 location(s) · Denali Therapeutics Inc. · NCT05371613A Natural History Study in Children With a Type II Collagen Disorder With Short Stature
Phase N/A · 2 location(s) · Innoskel · NCT05408715Longitudinal Study of Neurodegenerative Disorders
Phase N/A · 1 location(s) · University of Pittsburgh · NCT03333200Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
Phase 2 · 1 location(s) · Paul Szabolcs · NCT01962415
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This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.