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Condition: Leber Hereditary Optic Disease Synced from ClinicalTrials.gov · July 29, 2026

Recruiting studies: Leber Hereditary Optic Disease

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

New Non-invasive Modalities for Assessing Retinal Structure and Function
NA · 1 location(s) · Randy Kardon · NCT03475173North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
Phase N/A · 17 location(s) · Columbia University · NCT01694940Gene Therapy Clinical Trial for the Treatment Of Leber's HereDitary Optic Neuropathy
Phase 2/Phase 3 · 1 location(s) · Wuhan Neurophth Biotechnology Limited Company · NCT04912843Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Phase N/A · 2 location(s) · Sanford Health · NCT01793168Efficacy and Safety Study of Bilateral IVT Injection of GS010 at Two Dose Levels in LHON Patients
Phase 2 · 1 location(s) · GenSight Biologics · NCT07303296Metabolomics Analysis According to the Retinal Nerve Fiber Layer in Patients With NOHL Mutations (MétabOCT)
NA · 1 location(s) · Hôpital Necker-Enfants Malades · NCT06682819Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)
Phase 3 · 17 location(s) · Laboratoires Thea · NCT06891443Safety and Efficacy Trial of HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR)
Phase 1/Phase 2 · 3 location(s) · HuidaGene Therapeutics Co., Ltd. · NCT05906953Inherited Retinal Degenerative Disease Registry
Phase N/A · 1 location(s) · Foundation Fighting Blindness · NCT02435940Stem Cell Ophthalmology Treatment Study II
NA · 4 location(s) · MD Stem Cells · NCT03011541
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This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.