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Study identifier: NCT05906953 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

Safety and Efficacy Trial of HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR)

Condition: Leber Congenital Amaurosis · Inherited Retinal Diseases Caused by RPE65 Mutations  ·  Sponsor: HuidaGene Therapeutics Co., Ltd.

PhasePhase 1/Phase 2
Planned participants20
Who can joinAll sexes, 6 Years to 50 Years
Healthy volunteersNo

About this study

The purpose of the study is to determine whether HG004 as gene therapy is safe and effective for the treatment of Leber Congenital Amaurosis caused by mutations in RPE65 gene.

This description comes directly from the study's public registry record.

Talk to the study team

Study Director  ·  732-318-9873  ·  HG00402@huidagene.com

Always discuss trial participation with your own doctor first.

Locations (3)

Research SiteSacramento, California, United StatesRecruiting
Research SiteHouston, Texas, United StatesRecruiting
Research SiteShanghai, Shanghai Municipality, ChinaRecruiting

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Source record: clinicaltrials.gov/study/NCT05906953