Recruiting studies: Propionic Acidemia

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
Phase N/A · 32 location(s) · RECORDATI GROUP · NCT04176523 AAVrh10-PCCA Gene Therapy for Propionic Acidemia
Phase 1 · 1 location(s) · Mayo Clinic · NCT07643844 A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRN
Phase 1/Phase 2 · 22 location(s) · ModernaTX, Inc. · NCT05130437 Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
Phase N/A · 2 location(s) · National Human Genome Research Institute (NHGRI) · NCT02890342 An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
Phase N/A · 5 location(s) · RECORDATI GROUP · NCT05040178 Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Phase N/A · 2 location(s) · Sanford Health · NCT01793168 Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
Phase 1/Phase 2 · 35 location(s) · ModernaTX, Inc. · NCT04159103 A Retrospective Study to Characterize Participants With Propionic Acidemia
Phase N/A · 29 location(s) · ModernaTX, Inc. · NCT05769621

Look up another condition

Patient organization or foundation? You can brand this page for your community — your logo, your resources, same honest registry data, kept current daily. Ask about branding →

This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.