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Study identifier: NCT07281079 Synced from ClinicalTrials.gov · July 30, 2026
● Recruiting

A Study of NNZ-2591 in Pediatric Participants With Phelan-McDermid Syndrome

Condition: Phelan-McDermid Syndrome  ·  Sponsor: Neuren Pharmaceuticals Limited

PhasePhase 3
Planned participants160
Who can joinAll sexes, 3 Years to 12 Years
Healthy volunteersNo

About this study

This Phase 3, randomized, double-blind, parallel-group (2-arm), placebo-controlled, multicenter study will evaluate the efficacy and safety of NNZ-2591 compared to placebo in pediatric participants with Phelan- McDermid Syndrome.

This description comes directly from the study's public registry record.

Talk to the study team

Medical Information Lead  ·  231-203-8050  ·  medicalinformation@neurenpharma.com

Always discuss trial participation with your own doctor first.

Locations (12)

Neuren PMS-301 Site#122Glendale, California, United StatesRecruiting
Neuren PMS-301 Site #112Palo Alto, California, United StatesRecruiting
Neuren PMS-301 Site#103San Diego, California, United StatesRecruiting
Neuren PMS-301 Site#111San Rafael, California, United StatesRecruiting
Neuren PMS-301 Site#102Chicago, Illinois, United StatesRecruiting
Neuren PMS-301 Site#109Chevy Chase, Maryland, United StatesRecruiting
Neuren PMS-301 Site#106Brookline, Massachusetts, United StatesRecruiting
Neuren PMS-301 Site#104Lexington, Massachusetts, United StatesRecruiting
Neuren PMS-301 Site#101New York, New York, United StatesRecruiting
Neuren PMS-301 Site#108Cincinnati, Ohio, United StatesRecruiting
Neuren PMS-301 Site#115Houston, Texas, United StatesRecruiting
Neuren PMS-301 Site#201Toronto, Ontario, CanadaRecruiting

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Source record: clinicaltrials.gov/study/NCT07281079