Condition: Fabry Disease · Sponsor: Takeda
Fabry Disease is a rare blood disorder that some people are born with. People with Fabry disease have low levels of an enzyme called alpha-galactosidase A. This enzyme helps to cut down fat-like substances. Without alpha-galactosidase A, large forms of these substances build up and clot in blood vessels. Over time, this can affect vital organs (especially the heart, kidneys, and brain) causing serious health problems with advancing age. Agalsidase alfa (Replagal®) is a human enzyme made in the laboratory and may provide higher levels of alpha-galactosidase A. Replagal® works the same way as natural alpha-galactosidase A does. The main aim of this study is to learn more about the treatment with Replagal® in Chinese children and adults with Fabry disease. The study aims to assess the heart and kidney function in people with Fabry disease who are routinely treated with Replagal®. Other aims are to learn about the change in heart and kidney function, impact on quality of life, how the treatment with Replagal® works for people with Fabry Disease, and how safe the treatment with Replagal® is in routine real-world settings. Participants will receive with Replagal® per the routine treatment settings in China. No study-specific visits to the clinical are scheduled.
This description comes directly from the study's public registry record.
Takeda Contact · +1-877-825-3327 · medinfoUS@takeda.com
Always discuss trial participation with your own doctor first.
| The First Affiliated Hospital Of USTC (AnHui Provincial Hospital) | Hefei, Anhui, China | Not Yet Recruiting |
| Peking University First Hospital | Beijing, Beijing Municipality, China | Not Yet Recruiting |
| Peking University Third Hospital | Beijing, Beijing Municipality, China | Recruiting |
| Peking Union Medical College Hospital | Beijing, Beijing Municipality, China | Recruiting |
| Fuzhou University Provincial Affiliated Hospital | Fuzhou, Fujian, China | Recruiting |
| The Second Affiliated Hospital ZheJiang University School Of Medicine | Hangzhou, Guangdong, China | Not Yet Recruiting |
| ShanTou Central Hospital | Shantou, Guangdong, China | Recruiting |
| The University Of Hong Kong-ShenZhen Hospital | Shenzhen, Guangdong, China | Not Yet Recruiting |
| The Second Hospital of Hebei Medical University | Shijiazhuang, Hebei, China | Recruiting |
| The Second Affiliated Hospital of Harbin Medical University | Harbin, Heilongjiang, China | Not Yet Recruiting |
| Affiliated Drum Tower Hospital, Medical School of Nanjing University | Nanjing, Jiangsu, China | Recruiting |
| The First Affiliated Hospital With NanJing Medical University(JiangSu Province Hospital) | Nanjing, Jiangsu, China | Not Yet Recruiting |
+ 6 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT07187440