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Study identifier: NCT06975865 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

The Efficacy and Safety of Rilzabrutinib in Participants Aged 10 to 65 Years With Sickle-cell Disease

Condition: Sickle Cell Disease  ·  Sponsor: Sanofi

PhasePhase 3
Planned participants192
Who can joinAll sexes, 10 Years to 65 Years
Healthy volunteersNo

About this study

This is a multicenter, randomized, double-blind, placebo-controlled, parallel-group, flexible-adaptive, group-sequential study (Part A), followed by an open-label LTE period (Part B) to investigate the efficacy, and safety of rilzabrutinib in participants with sickle-cell disease (SCD). Study details include: * Study duration: a 52-week double-blind period (Part A), followed by an open-label LTE period (Part B). Double-blind period has two parts, 50% (adult only) until the interim analysis (a proof-concept part analogous to a phase 2b study), and 50% (adult and children) after the interim analysis. Only the participants who complete double-blind treatment period (Part A) are eligible to continue to the LTE period. The duration of the LTE period (Part B) will be from the first-participant-in (FPI)-LTE (Part B) until the last participant who enters the LTE has completed 52 weeks. * Treatment duration: 52-week double-blind period (Part A); LTE period (Part B) from the (FPI until the last participant who enters the LTE has completed 52 weeks. * Visit frequency: Week visits based on the Schedule of Assessments.

This description comes directly from the study's public registry record.

Talk to the study team

Trial Transparency email recommended (Toll free for US & Canada)  ·  800-633-1610  ·  contact-us@sanofi.com

Always discuss trial participation with your own doctor first.

Locations (53)

University of Alabama at Birmingham- Site Number : 8400003Birmingham, Alabama, United StatesRecruiting
Phoenix Children's Hospital- Site Number : 8400028Phoenix, Arizona, United StatesRecruiting
University of California San Francisco- Site Number : 8400040Fresno, California, United StatesRecruiting
Oncology & Hematology Associates of West Broward- Site Number : 8400029Coral Springs, Florida, United StatesRecruiting
Sylvester Comprehensive Cancer Center- Site Number : 8400020Miami, Florida, United StatesRecruiting
University of Illinois-Chicago - College of Medicine- Site Number : 8400054Chicago, Illinois, United StatesRecruiting
Indiana University Health Riley Hospital for Children- Site Number : 8400056Indianapolis, Indiana, United StatesRecruiting
Louisiana State University Health Sciences Center - Shreveport- Site Number : 8400037Shreveport, Louisiana, United StatesRecruiting
University of Maryland School of Medicine - Baltimore- Site Number : 8400041Baltimore, Maryland, United StatesRecruiting
University of Michigan Health System - Ann Arbor- Site Number : 8400035Ann Arbor, Michigan, United StatesRecruiting
Southern Specialty Research- Site Number : 8400059Flowood, Mississippi, United StatesRecruiting
Richmond University Medical Center- Site Number : 8400038Staten Island, New York, United StatesRecruiting

+ 41 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT06975865