Condition: Hemophilia A · Hemophilia B · Sponsor: St. Jude Children's Research Hospital
This observational study will obtain liver biopsy samples and evaluate the long-term effect of adeno-associated virus (AAV)-mediated gene therapy on the liver tissue in adult patients with hemophilia A or hemophilia B who have previously been treated with a factor VIII or factor IX gene-containing AAV-vector for liver-targeted gene transfer. Participants are from a cohort of patients treated with AAV-mediated gene transfer and at least 6 months after vector infusion.
This description comes directly from the study's public registry record.
Ulrike Reiss, MD · 888-226-4343 · referralinfo@stjude.org
Always discuss trial participation with your own doctor first.
| St. Jude Children's Research Hospital | Memphis, Tennessee, United States | — |
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