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Study identifier: NCT05476939 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

Biological Medicine for Diffuse Intrinsic Pontine Glioma (DIPG) Eradication 2.0

Condition: Diffuse Intrinsic Pontine Glioma · Diffuse Midline Glioma, H3 K27M-Mutant · Diffuse Midline Glioma, H3K27-altered  ·  Sponsor: Gustave Roussy, Cancer Campus, Grand Paris

PhasePhase 3
Planned participants433
Who can joinAll sexes, 6 Months to no upper limit
Healthy volunteersNo

About this study

The BIOMEDE 2.0 study is the second stage of the BIOMEDE multi-arm, multistage rolling programme (adaptive platform protocol). It is a multicenter, randomized, open-label, controlled phase-3 trial evaluating efficacy of ONC201 in comparison with everolimus (primary objective based on internal comparison) and subsequently to historical controls. Two treatment groups will be compared. A switch between treatment groups is allowed after confirmation of the disease progression (real-time central review blinded to the treatment arm allocation). Study treatment will be continued until centrally confirmed disease progression (either radiologically or histologically), unacceptable toxicity or consent withdrawal. The final conclusion of the trial will be successful for ONC201, if ONC201 is found significantly superior to everolimus in terms of centrally-reviewed PFS (Progression-free survival) from randomization (internal comparison) either overall, considering ND-DMG and DIPG-patients together, or in the subgroup of ND-DMG patients alone. In other cases, Everolimus will remain the standard arm unless it appears associated with an excess of toxicity compared to ONC201 which could then be discussed as a new standard.

This description comes directly from the study's public registry record.

Talk to the study team

Jacques GRILL, MD, PhD  ·  +33 (0)1 42 11 62 09  ·  jacques.grill@gustaveroussy.fr

Anne-Sophie BLANC, PharmD  ·  +33 (0)1 42 11 57 02  ·  annesophie.blanc@gustaveroussy.fr

Always discuss trial participation with your own doctor first.

Locations (50)

Aarhus Universitetshospital SkejbyAarhus, DenmarkRecruiting
RigshospitaletCopenhagen, DenmarkRecruiting
H.C. Andersen Children's Hospital, Odense UniversitetshospitalOdense, DenmarkRecruiting
Gustave RoussyVillejuif, Val de Marne, FranceRecruiting
CHU d'Amiens-Picardie Site SudAmiens, FranceRecruiting
Institut de Cancérologie de l'Ouest (ICO) - Site Paul PapinAngers, FranceRecruiting
CHU d'Angers - Bâtiment Robert DebréAngers, FranceRecruiting
CHU Besançon - Hôpital Jean MinjozBesançon, FranceRecruiting
CHU de Bordeaux - Groupe hospitalier Saint André - Hôpital Saint AndréBordeaux, FranceRecruiting
CHU de Bordeaux - Groupe hospitalier Pellegrin - Hôpital des enfantsBordeaux, FranceRecruiting
CHRU de Brest - Hôpital MorvanBrest, FranceRecruiting
CHU de Caen - Hôpital Côte de NacreCaen, FranceRecruiting

+ 38 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT05476939