EICHOR
● Completed
A Study of Intrathecal SHP611 in Children With Metachromatic Leukodystrophy
Condition: Metachromatic Leukodystrophy (MLD) · Sponsor: Shire
About this study
The main aim of the study is to determine if SHP611 given by injection into the spinal fluid that surrounds the brain and spinal cord (intrathecal; IT) prolongs the time for children with Metachromatic Leukodystrophy (MLD) to retain the ability to move from place to place. Other aims of the study are to determine the effects of intrathecal administration of SHP611 on movement and speech functions and to learn how well SHP611 injected in the spinal fluid that surrounds the brain and spinal cord is tolerated. Study participants will receive SHP611 for about 2 years with the possibility of an extended treatment period.
This description comes directly from the study's public registry record.
Talk to the study team
No contact information is available for this study as per the public registry record.
Always discuss trial participation with your own doctor first.
Locations (30)
| Los Angeles Biomedical Research Institute at Harbor-UCLA | Torrance, California, United States | — |
| Childrens Hospital Colorado | Aurora, Colorado, United States | — |
| Rare Disease Research, LLC | Atlanta, Georgia, United States | — |
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago, Illinois, United States | — |
| University of Iowa Stead Family Children's Hospital | Iowa City, Iowa, United States | — |
| Mayo Clinic - PPDS | Rochester, Minnesota, United States | — |
| New York University Langone Medical Center | New York, New York, United States | — |
| Cincinnati Children's Hospital Medical Center | Cincinnati, Ohio, United States | — |
| Children's Hospital of Philadelphia | Philadelphia, Pennsylvania, United States | — |
| Children's Hospital of Pittsburgh | Pittsburgh, Pennsylvania, United States | — |
| University of Utah | Salt Lake City, Utah, United States | — |
| Hospital Universitario Austral - PIN | Ciudad Autónoma Buenos Aires, Buenos Aires, Argentina | — |
+ 18 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT03771898