Recruiting studies: Spinal Muscular Atrophy Type I

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

Exploring Bulbar Function, Speech And Communication Development in SMA Type 1
Phase N/A · 1 location(s) · Institute of Child Health · NCT05954455 UK SMA Patient Registry
Phase N/A · 1 location(s) · Newcastle University · NCT04292574 Evaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular Atrophy
NA · 4 location(s) · Centre Hospitalier Universitaire de Saint Etienne · NCT06562283 Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1
Phase 1/Phase 2 · 1 location(s) · Gemma Biotherapeutics · NCT07070999 Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Phase N/A · 2 location(s) · Sanford Health · NCT01793168 Test of Aquatic Mobility of SMA Infants
NA · 1 location(s) · Assistance Publique - Hôpitaux de Paris · NCT06152302 Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients
Phase 1/Phase 2 · 4 location(s) · GeneCradle Inc · NCT05824169 Assessing the Fertility Status of Men With Spinal Muscular Atrophy (SMA)
Phase N/A · 1 location(s) · Bar-Chama, Natan, M.D. · NCT06194539

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This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.