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Condition: Mps Iiia Synced from ClinicalTrials.gov · July 29, 2026

Recruiting studies: Mps Iiia

Studies currently listed as recruiting on the public registry for this search term. Each page explains the study in plain language, with locations and the study team's contact details. Clinicians: generate a printable list for your patient →

Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH
Phase 2/Phase 3 · 5 location(s) · Ultragenyx Pharmaceutical Inc · NCT02716246
Phase 1 Study of GC1130A in Patients With Sanfilippo Syndrome Type A (MPS IIIA)
Phase 1 · 5 location(s) · GC Biopharma Corp · NCT06567769
An Open Label Dose Escalation Study to Assess the Safety, Tolerability, and Pharmacologic Properties of High Dose Ambrox
Phase 2/Phase 3 · 1 location(s) · Ozlem Goker-Alpan · NCT06614894
Longitudinal Study of Neurodegenerative Disorders
Phase N/A · 1 location(s) · University of Pittsburgh · NCT03333200
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This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.