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Study identifier: NCT07549698 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

Safety and Preliminary Efficacy of CTX112 in Adult Participants With Relapsed/Refractory Hematologic Autoimmune Disease

Condition: Warm Autoimmune Hemolytic Anemia (WAIHA) · ITP - Immune Thrombocytopenia · Warm Autoimmune Hemolytic Anemia  ·  Sponsor: CRISPR Therapeutics AG

PhasePhase 1/Phase 2
Planned participants60
Who can joinAll sexes, 18 Years to no upper limit
Healthy volunteersNo

About this study

This is a single-arm, open-label, multicenter, ascending dose Phase 1/2 trial evaluating the safety and preliminary efficacy of CTX112 or Zugocabtagene geleucel (zugo-cel) in adult participants with relapsed/refractory primary Immune Thrombocytopenia (ITP) and relapsed/refractory primary Warm Autoimmune Hemolytic Anemia (wAIHA).

This description comes directly from the study's public registry record.

Talk to the study team

Clinical Trials  ·  877-214-4634  ·  medicalaffairs@crisprtx.com

Always discuss trial participation with your own doctor first.

Locations (10)

Mayo Clinic in RochesterRochester, Minnesota, United StatesRecruiting
University of Nebraska Medical CenterOmaha, Nebraska, United StatesRecruiting
Universitaetsklinikum KoelnCologne, GermanyRecruiting
Medizinische Hochschule HannoverHannover, GermanyNot Yet Recruiting
Medizinische Hochschule Hannover (MHH)Hanover, GermanyNot Yet Recruiting
UCT University Medical Center MainzMainz, GermanyNot Yet Recruiting
Hospital Universitario Reina SofiaCórdoba, SpainRecruiting
Gregorio Marañón General University HospitalMadrid, SpainRecruiting
Hospital Universitario La PazMadrid, SpainNot Yet Recruiting
Hospital Universitario Virgen del RocioSeville, SpainRecruiting

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Source record: clinicaltrials.gov/study/NCT07549698