Condition: Achondroplasia · Sponsor: BioMarin Pharmaceutical
This is a multicenter, multinational, randomized, active-controlled, operationally seamless Phase 2/3 study of BMN 333 in treatment-naïve pediatric participants with achondroplasia (ACH). The study consists of a Phase 2 part and a Phase 3 part.
This description comes directly from the study's public registry record.
Trial Specialist · 1-800-983-4587 · medinfo@bmrn.com
Study Manager · 1-800-983-4587 · Medinfo@bmrn.com
Always discuss trial participation with your own doctor first.
| UCSF Benioff Children's Hospital Oakland | Oakland, California, United States | Recruiting |
| Nemours Children's Health | Wilmington, Delaware, United States | Not Yet Recruiting |
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago, Illinois, United States | Recruiting |
| Johns Hopkins Medicine | Baltimore, Maryland, United States | Recruiting |
| Cincinnati Children's Hospital Medical Center | Cincinnati, Ohio, United States | Not Yet Recruiting |
| Children's Hospital of Philadelphia | Philadelphia, Pennsylvania, United States | Not Yet Recruiting |
| University of Texas Southwestern Medical Center | Dallas, Texas, United States | Not Yet Recruiting |
| Texas Children Hospital, Baylor College of Medicine | Houston, Texas, United States | Recruiting |
| Consano Clinical Research, LLC | San Antonio, Texas, United States | Recruiting |
| Murdoch Children's Research Institute | Parkville, Victoria, Australia | Recruiting |
| Universite de Montreal - Centre Hospitalier Universitaire Sainte-Justine | Montreal, Quebec, Canada | Not Yet Recruiting |
| Irccs Ospedale Gaslini Di Genova | Genova, Italy | Not Yet Recruiting |
+ 7 more locations — full list on the registry record.
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This page is independently generated by Eichor from the public ClinicalTrials.gov record and re-synced daily. It is not the sponsor's official website unless claimed. Nothing here is medical advice; eligibility is always determined by the study team — talk to your own doctor first.
Source record: clinicaltrials.gov/study/NCT07441876