Condition: Alagille Syndrome · Progressive Familial Intrahepatic Cholestasis · Sponsor: Mirum Pharmaceuticals, Inc.
In patients with Alagille syndrome (ALGS), the key objectives are to evaluate the tolerability, long-term safety (including possible liver toxicity) and long-term efficacy of Livmarli treatment. In patients with Progressive Familial Intrahepatic Cholestasis (PFIC), the key objectives are to evaluate tolerability, long-term safety (including possible liver toxicity and potential impact of chronic exposure to propylene glycol (PG)), long-term efficacy, and growth and development.
This description comes directly from the study's public registry record.
Clinical Trials Mirum · +16506674085 · clinicaltrials@mirumpharma.com
Always discuss trial participation with your own doctor first.
| Cliniques Universitaires Saint Luc (UCLouvain) | Brussels, Belgium | Recruiting |
| University Hospital Gent (UZ Gent) | Ghent, Belgium | Recruiting |
| Hospices Civils de Lyon - Hopital Femme Mère Enfant | Bron, Auvergne-Rhône-Alpes, France | Recruiting |
| CHU de Toulouse - Hôpital des Enfants | Toulouse, Occitanie, France | Recruiting |
| Bicetre University Hospital | Le Kremlin-Bicêtre, Île-de-France Region, France | Recruiting |
| Charite Berlin | Berlin, Germany | Recruiting |
| Children's University Hospital Essen | Essen, Germany | Recruiting |
| University Hospital Hamburg-Eppendorf | Hamburg, Germany | Recruiting |
| 2nd Paediatric Clinic P &A Kyriakou Children's Hospital | Athens, Greece | Not Yet Recruiting |
| AO Ospedale PAPA GIOVANNI XXIII | Bergamo, Lombardy, Italy | Recruiting |
| Istituto mediterraneo trapianti - ISMETT | Palermo, Sicily, Italy | Recruiting |
| University Medical Center Groningen (UMCG) | Groningen, Netherlands | Recruiting |
+ 3 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT07290257