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Study identifier: NCT07223944 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

A Gaucher Disease Gene Therapy Trial With FLT201

Condition: Gaucher Disease Type 1  ·  Sponsor: Spur Therapeutics

PhasePhase 3
Planned participants45
Who can joinAll sexes, 18 Years to no upper limit
Healthy volunteersNo

About this study

This study is a Phase 3, non-randomized, multicenter, efficacy and safety study in adult patients with Gaucher disease Type 1, on stable treatment with enzyme replacement therapy (ERT) or substrate reduction therapy (SRT) for at least 2 years. The study aims to confirm the efficacy and safety of FLT201 in this population after discontinuation of ERT/SRT.

This description comes directly from the study's public registry record.

Talk to the study team

Spur Clinical Trials Contact  ·  +44 (0)1438 906870  ·  clinicaltrials@spurtherapeutics.com

Always discuss trial participation with your own doctor first.

Locations (33)

Kaiser Permanente - CALos Angeles, California, United StatesRecruiting
UCLA HealthLos Angeles, California, United StatesNot Yet Recruiting
University of California, San Francisco (UCSF)San Francisco, California, United StatesRecruiting
University of Colorado AnschutzAurora, Colorado, United StatesRecruiting
Emory HealthcareAtlanta, Georgia, United StatesNot Yet Recruiting
University of Iowa Health CareIowa City, Iowa, United StatesNot Yet Recruiting
University of MinnesotaMinneapolis, Minnesota, United StatesRecruiting
Hackensack University Medical CenterHackensack, New Jersey, United StatesNot Yet Recruiting
NYU Langone HealthNew York, New York, United StatesNot Yet Recruiting
Columbia UniversityNew York, New York, United StatesNot Yet Recruiting
Duke University Medical CenterDurham, North Carolina, United StatesRecruiting
Cincinnati Children's Hospital Medical CenterCincinnati, Ohio, United StatesNot Yet Recruiting

+ 21 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT07223944