Condition: Turner Syndrome · Short Stature Homeobox Gene Mutation · Idiopathic Short Stature · Sponsor: Ascendis Pharma A/S
This basket trial will enroll prepubertal children and adolescents with clinically diagnosed and genetically confirmed (if applicable) TS, SHOX-D, SGA, or ISS between ages of ≥2 and \<18 years with open growth plates. The purpose of the study is to see how well treatment with once-weekly lonapegsomatropin works compared to treatment with daily somatropin. Approximately 186 participants will be distributed equally (1:1), to receive either lonapegsomatropin for 2 years or somatropin for 1 year followed by lonapegsomatropin for 1 year. This trial will be conducted in the United States, France, Germany, Italy, Romania, Spain and South Korea.
This description comes directly from the study's public registry record.
Ascendis Registry Inquiries · +4561161658 · asnd_registryinquiries@ascendispharma.com
Always discuss trial participation with your own doctor first.
| Ascendis Pharma Investigational Site | Palo Alto, California, United States | Recruiting |
| Ascendis Pharma Investigational Site | Sacramento, California, United States | Recruiting |
| Ascendis Pharma Investigational Site | Aurora, Colorado, United States | Recruiting |
| Ascendis Pharma Investigational Site | Centennial, Colorado, United States | Recruiting |
| Ascendis Pharma Investigational Site | Orlando, Florida, United States | Recruiting |
| Ascendis Pharma Investigational Site | St. Petersburg, Florida, United States | Recruiting |
| Ascendis Pharma Investigational Site | Atlanta, Georgia, United States | Recruiting |
| Ascendis Pharma Investigational Site | Idaho Falls, Idaho, United States | Recruiting |
| Ascendis Pharma Investigational Site | New Orleans, Louisiana, United States | Recruiting |
| Ascendis Pharma Investigational Site | Minneapolis, Minnesota, United States | Recruiting |
| Ascendis Pharma Investigational Site | Saint Paul, Minnesota, United States | Recruiting |
| Ascendis Pharma Investigational Site | Lake Success, New York, United States | Recruiting |
+ 22 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT07221851