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Study identifier: NCT07159841 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH)

Condition: Congenital Adrenal Hyperplasia · Classic Congenital Adrenal Hyperplasia  ·  Sponsor: Crinetics Pharmaceuticals Inc.

PhasePhase 2/Phase 3
Planned participants153
Who can joinAll sexes, 1 Year to 17 Years
Healthy volunteersNo

About this study

The purpose of this study is to evaluate the safety, efficacy, pharmacokinetics (PK), and pharmacodynamics (PD) of atumelnant treatment in pediatric participants with classic congenital adrenal hyperplasia (CAH).

This description comes directly from the study's public registry record.

Talk to the study team

Crinetics Clinical Trials  ·  833-827-9741  ·  clinicaltrials@crinetics.com

Always discuss trial participation with your own doctor first.

Locations (43)

UCSF Ron Conway Gateway Medical BuildingSan Francisco, California, United StatesRecruiting
Boston's Children's HospitalBoston, Massachusetts, United StatesRecruiting
University of MichiganAnn Arbor, Michigan, United StatesRecruiting
University of MinnesotaMinneapolis, Minnesota, United StatesRecruiting
Rutgers Robert Wood Johnson Medical SchoolNew Brunswick, New Jersey, United StatesRecruiting
Icahn School of Medicine at Mount Sinai-Mount Sinai HospitalNew York, New York, United StatesRecruiting
Children's Hospital of PhiladelphiaPhiladelphia, Pennsylvania, United StatesRecruiting
Cook Children's Health Care SystemFort Worth, Texas, United StatesRecruiting
University of Virginia Health SystemCharlottesville, Virginia, United StatesRecruiting
Instituto de Investigaciones MetabólicasBuenos Aires, Buenos Aires, ArgentinaRecruiting
Hospital de Niños de la Santísima TrinidadCórdoba, Córdoba Province, ArgentinaRecruiting
Hospital Italiano de Buenos AiresBuenos Aires, ArgentinaRecruiting

+ 31 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT07159841