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Study identifier: NCT07154745 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

A Study to Evaluate How Pozelimab + Cemdisiran Combination Therapy Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Whose Current Treatment is Not Working Efficiently

Condition: Paroxysmal Nocturnal Hemoglobinuria  ·  Sponsor: Regeneron Pharmaceuticals

PhasePhase 3
Planned participants35
Who can joinAll sexes, 18 Years to no upper limit
Healthy volunteersNo

About this study

This study is researching a treatment combination with two experimental drugs called pozelimab and cemdisiran referred to as "study drugs". Researchers are looking for a better way to treat Paroxysmal Nocturnal Hemoglobinuria (PNH). The aim of the study is to see how well the pozelimab and cemdisiran combination works to lower hemolysis in participants whose PNH has been not well controlled even after taking other complement component 5 (C5) inhibitors, eculizumab/eculizumab biosimilar, ravulizumab or crovalimab. The study is looking at several other research questions, including: * What side effects may happen from taking the study drugs? * How much of the study drugs are in the blood at different times? * Whether the body makes antibodies against the study drug (which could make the study drugs not work as well or could lead to side effects)

This description comes directly from the study's public registry record.

Talk to the study team

Clinical Trials Administrator  ·  844-734-6643  ·  clinicaltrials@regeneron.com

Always discuss trial participation with your own doctor first.

Locations (19)

Hospital das Clinicas da FMRP USPRibeirão Preto, São Paulo, BrazilRecruiting
Faculdade de Medicina do ABCSanto André, São Paulo, BrazilRecruiting
CISSS-CALévis, Quebec, CanadaRecruiting
Universita Cattolica del Sacro Cuore - Policlinico Universitario A. GemelliRome, Lazio, ItalyRecruiting
AOU CareggiFlorence, Tuscany, ItalyRecruiting
SC Hematology, AOU Città della Salute e della Scienza di TorinoTorino, ItalyRecruiting
In-Vivo Sp. z o.o.Bydgoszcz, Kuyavian-Pomeranian Voivodeship, PolandRecruiting
Seoul National University HospitalSeoul, South KoreaRecruiting
Severance HospitalSeoul, South KoreaRecruiting
Seoul St. Mary's Hospital - The Catholic University of KoreaSeoul, South KoreaRecruiting
Ewha Womans University Mokdong HospitalSeoul, South KoreaRecruiting
Samsung Medical CenterSeoul, South KoreaRecruiting

+ 7 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT07154745