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Study identifier: NCT07002398 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

Safety and Preliminary Efficacy of VG801 in Patients With ABCA4 Mutation-associated Retinal Dystrophy (Stargardt Disease)

Condition: Retinal Dystrophy Due to Biallelic ABCA4 Mutations · Stargardt Disease 1  ·  Sponsor: VeonGen Therapeutics GmbH

PhasePhase 1/Phase 2
Planned participants15
Who can joinAll sexes, 6 Years to no upper limit
Healthy volunteersNo

About this study

This is a single-arm, open-label, non-randomized, single dose-escalation, first-in-human (FIH) clinical trial to evaluate the safety and preliminary efficacy of VG801 for treatment of patients with retinal dystrophy (Stargardt disease) due to biallelic ABCA4 mutations.

This description comes directly from the study's public registry record.

Talk to the study team

Research Coordinator  ·  +86-021-36123569  ·  shiyilunli@sina.com

Always discuss trial participation with your own doctor first.

Locations (1)

Shanghai General HospitalShanghai, Shanghai Municipality, ChinaRecruiting

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Source record: clinicaltrials.gov/study/NCT07002398