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Study identifier: NCT06838676 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

ACT001 for the Treatment of Diffuse Intrinsic Pontine Gliomas and H3K27-altered High Grade Gliomas

Condition: Diffuse Intrinsic Pontine Gliomas (DIPG) · Progressive DIPG · Refractory DIPG  ·  Sponsor: Nationwide Children's Hospital

PhasePhase 2
Planned participants60
Who can joinAll sexes, 12 Months to 39 Years
Healthy volunteersNo

About this study

This is a Phase II open-label study to investigate the safety and efficacy of ACT001 in patients with DIPG and H3K27-altered HGG.

This description comes directly from the study's public registry record.

Talk to the study team

Kelsey H Troyer, PhD  ·  16147223284  ·  kelsey.troyer@nationwidechildrens.org

Always discuss trial participation with your own doctor first.

Locations (20)

Children's Hospital ColoradoAurora, Colorado, United StatesRecruiting
Children's National Medical CenterWashington D.C., District of Columbia, United StatesRecruiting
Nicklaus Children's HospitalMiami, Florida, United StatesNot Yet Recruiting
Emory University/Children's Healthcare of AtlantaAtlanta, Georgia, United StatesNot Yet Recruiting
C.S. Mott Children's HospitalAnn Arbor, Michigan, United StatesNot Yet Recruiting
St. Louis Children's HospitalSt Louis, Missouri, United StatesNot Yet Recruiting
Duke University Medical CenterDurham, North Carolina, United StatesNot Yet Recruiting
Cincinnati Children's HospitalCincinnati, Ohio, United StatesRecruiting
Nationwide Children's HospitalColumbus, Ohio, United StatesRecruiting
Children's Hospital of PhilidelphiaPhilidelphia, Pennsylvania, United StatesNot Yet Recruiting
Texas Children's HospitalHouston, Texas, United StatesRecruiting
Seattle Children's HospitalSeattle, Washington, United StatesRecruiting

+ 8 more locations — full list on the registry record.

Follow this study

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Source record: clinicaltrials.gov/study/NCT06838676