Condition: Noonan Syndrome · Sponsor: BioMarin Pharmaceutical
The purpose of this study in children with Noonan syndrome is to evaluate the effect of 3 doses of vosoritide on growth as measured by AGV after 6 months of treatment. The long-term efficacy and safety of vosoritide at the therapeutic dose will be evaluated up to FAH.
This description comes directly from the study's public registry record.
Trial Specialist · 1-800-983-4587 · medinfo@bmrn.com
Study Manager · 1-800-983-4587 · Medinfo@bmrn.com
Always discuss trial participation with your own doctor first.
| Childrens Hospital Los Angeles | Los Angeles, California, United States | Recruiting |
| Children's Hospital of Orange County Main Campus - Orange | Orange, California, United States | Recruiting |
| Children's Hospital Colorado | Aurora, Colorado, United States | Recruiting |
| Nemours Children's Hospital, Delaware (Alfred I. Dupont Hospital for Children) | Wilmington, Delaware, United States | Recruiting |
| Children's National Medical Center | Washington D.C., District of Columbia, United States | Recruiting |
| Nicklaus Children's Hospital | Miami, Florida, United States | Not Yet Recruiting |
| Emory University School of Medicine | Atlanta, Georgia, United States | Recruiting |
| St. Luke's Children's Endocrinology and Diabetes | Boise, Idaho, United States | Recruiting |
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago, Illinois, United States | Recruiting |
| Riley Hospital for Children at Indiana University Health | Indianapolis, Indiana, United States | Recruiting |
| University of Iowa | Iowa City, Iowa, United States | Recruiting |
| Kentucky Children's Hospital | Lexington, Kentucky, United States | Recruiting |
+ 24 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT06668805