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Study identifier: NCT06663358 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

Condition: Fabry Disease  ·  Sponsor: Chiesi Farmaceutici S.p.A.

PhaseN/A
Planned participants100
Who can joinAll sexes, 18 Years to no upper limit
Healthy volunteersNo

About this study

A multi-centre, multi-country, observational, non-interventional, retrospective and prospective (hybrid) study among Fabry disease participants treated with pegunigalsidase alfa (Elfabrio®) in routine clinical care.

This description comes directly from the study's public registry record.

Talk to the study team

Medical Information Chiesi  ·  (888) 661-9260  ·  us.medical@chiesi.com

Always discuss trial participation with your own doctor first.

Locations (10)

University of Alabama at BirminghamBirmingham, Alabama, United StatesRecruiting
Emory University School of MedicineAtlanta, Georgia, United StatesRecruiting
Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of ChicagoChicago, Illinois, United StatesRecruiting
University of Iowa Hospitals and ClinicsIowa City, Iowa, United StatesRecruiting
Infusion AssociatesGrand Rapids, Michigan, United StatesRecruiting
Lysosomal & Rare Disorder Research & Treatment Center (LRDRTC)Fairfax, Virginia, United StatesRecruiting
General Hospital Slovenj GradecSlovenj Gradec, SloveniaRecruiting
University Hospitals Birmingham NHS Foundation Trust, Queen Elizabeth HospitalEdgbaston, Birmingham, United KingdomRecruiting
Salford RoyalSalford, Greater Manchester, United KingdomRecruiting
The Royal Free HospitalLondon, United KingdomRecruiting

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Source record: clinicaltrials.gov/study/NCT06663358