Condition: Duchenne Muscular Dystrophy · Sponsor: Catalyst Pharmaceuticals, Inc.
The goal of this study is to collect additional information on the safety of long-term treatment with AGAMREE® and to explore long-term clinical impact of AGAMREE® on quality of life, as assessed by standardized patient-reported outcome measures (QoL questionnaires) in male patients aged 2 years and older with Duchenne muscular dystrophy (DMD).
This description comes directly from the study's public registry record.
Mark Wingertzahn, PhD · (305) 420-3200 · mark.wingertzahn@catalystpharma.com
Always discuss trial participation with your own doctor first.
| Phoenix Children's Hospital | Phoenix, Arizona, United States | Recruiting |
| Arkansas Childrens Hospital | Little Rock, Arkansas, United States | Recruiting |
| Loma Linda University Pediatric Subspecialty Clinics | Loma Linda, California, United States | Not Yet Recruiting |
| Children's Hospital Los Angeles | Los Angeles, California, United States | Not Yet Recruiting |
| Valley Children's Hospital | Madera, California, United States | Not Yet Recruiting |
| Stanford University | Palo Alto, California, United States | Not Yet Recruiting |
| University of California, Davis | Sacramento, California, United States | Not Yet Recruiting |
| Children's National Health System | Washington D.C., District of Columbia, United States | Not Yet Recruiting |
| University of Florida Clinical and Translational Science Institue | Gainesville, Florida, United States | Not Yet Recruiting |
| University of Miami | Miami, Florida, United States | Not Yet Recruiting |
| Nicklaus Children's Hospital | Miami, Florida, United States | Recruiting |
| Nemours Children's Hospital | Orlando, Florida, United States | Recruiting |
+ 21 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT06564974