Condition: Paroxysmal Nocturnal Hemoglobinuria · PNH · Extravascular Hemolysis · Sponsor: Alexion Pharmaceuticals, Inc.
The primary objective of this study is to evaluate efficacy of danicopan as add-on treatment to ravulizumab or eculizumab as assessed by hemoglobin (Hgb) change from Baseline at Week 12 in pediatric participants with paroxysmal nocturnal hemoglobinuria (PNH) and clinically significant extravascular hemolysis (CS-EVH).
This description comes directly from the study's public registry record.
Alexion Pharmaceuticals, Inc. (Sponsor) · 1-855-752-2356 · clinicaltrials@alexion.com
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| Research Site | Saskatoon, Saskatchewan, Canada | Recruiting |
| Research Site | Paris, France | Recruiting |
| Research Site | Leeds, United Kingdom | Recruiting |
| Research Site | London, United Kingdom | Recruiting |
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Source record: clinicaltrials.gov/study/NCT06449001