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Study identifier: NCT06382155 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

A Phase 2 Study of Vosoritide in Children With Idiopathic Short Stature

Condition: Idiopathic Short Stature  ·  Sponsor: BioMarin Pharmaceutical

PhasePhase 2
Planned participants100
Who can joinAll sexes, 3 Years to 11 Years
Healthy volunteersNo

About this study

The purpose of this study is to evaluate i) the effect of multiple doses of vosoritide and ii) the effect of the therapeutic dose of vosoritide compared to human growth hormone (hGH)(hGH; only in the United States), in children with idiopathic short stature (ISS).

This description comes directly from the study's public registry record.

Talk to the study team

Trial Specialist  ·  +1 415.475.5852  ·  medinfo@bmrn.com

Always discuss trial participation with your own doctor first.

Locations (47)

Consano Clinical Research, LLCCalifornia City, California, United StatesRecruiting
Rady Children's Hospital - San DiegoCalifornia City, California, United StatesRecruiting
Children's Hospital of Orange County Main Campus - OrangeCalifornia City, California, United StatesRecruiting
Children's Hospital Los AngelesLos Angeles, California, United StatesRecruiting
Children's Hospital Oakland Research InstituteOakland, California, United StatesRecruiting
Center Of Excellence in Diabetes and EndocrinologySacramento, California, United StatesRecruiting
Lundquist Institute for Biomedical Innovation (LA BioMed)Torrance, California, United StatesRecruiting
The Children's National Research InstituteWashington D.C., District of Columbia, United StatesRecruiting
Nemours Children's Specialty Care JacksonvilleJacksonville, Florida, United StatesRecruiting
Nicklaus Children's HospitalMiami, Florida, United StatesRecruiting
Optimal Research SitesOrange City, Florida, United StatesRecruiting
Nemours Children's Health System - Corporate HeadquartersPensacola, Florida, United StatesRecruiting

+ 35 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT06382155