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Study identifier: NCT06212947 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

A Multicenter Multinational Observational Study of Children With Hypochondroplasia

Condition: Hypochondroplasia  ·  Sponsor: BioMarin Pharmaceutical

PhaseN/A
Planned participants400
Who can joinAll sexes, N/A to 15 Years
Healthy volunteersNo

About this study

This study will assess growth over time and the clinical course of HCH in children by collecting growth measurements and other variables of interest.

This description comes directly from the study's public registry record.

Talk to the study team

Trial Specialist  ·  1-800-983-4587  ·  medinfo@bmrn.com

Always discuss trial participation with your own doctor first.

Locations (43)

Phoenix Children's HospitalPhoenix, Arizona, United StatesRecruiting
Cedars-Sinai Medical CenterLos Angeles, California, United StatesNot Yet Recruiting
UCSF Benioff Children's HospitalOakland, California, United StatesRecruiting
Nemours Alfred I. Dupont Hospital for ChildrenWilmington, Delaware, United StatesRecruiting
Children's National Health SystemWashington D.C., District of Columbia, United StatesRecruiting
Ann & Robert H. Lurie Children's Hospital of ChicagoChicago, Illinois, United StatesRecruiting
The Johns Hopkins University School of MedicineBaltimore, Maryland, United StatesNot Yet Recruiting
Boston Children's HospitalBoston, Massachusetts, United StatesRecruiting
University of Minnesota Masonic Children's HospitalMinneapolis, Minnesota, United StatesRecruiting
University of MissouriColumbia, Missouri, United StatesRecruiting
Washington University School of Medicine in St. LouisSt Louis, Missouri, United StatesRecruiting
Mount Sinai Kravis Children's HospitalNew York, New York, United StatesRecruiting

+ 31 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT06212947