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Study identifier: NCT06023641 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

Treatment of Newly Diagnosed Rhabdomyosarcoma Using Molecular Risk Stratification and Liposomal Irinotecan Based Therapy in Children With Intermediate and High Risk Disease

Condition: Rhabdomyosarcoma  ·  Sponsor: St. Jude Children's Research Hospital

PhasePhase 2
Planned participants135
Who can joinAll sexes, N/A to 22 Years
Healthy volunteersNo

About this study

This is a phase II study to determine safety and efficacy of combining liposomal irinotecan with vincristine alternating with VAC in intermediate-risk patients, liposomal irinotecan with temozolomide and vincristine alternating with VAC in high-risk patients and the chemotherapy combinations when given with concomitant radiation therapy in intermediate and high risk patients. Primary Objective * Estimate event-free survival for intermediate-risk participants treated with VAC and vincristine and liposomal irinotecan (VLI) with the addition of maintenance therapy with vinorelbine and cyclophosphamide. * Estimate the event-free survival for high-risk patients treated with VAC and vincristine, liposomal irinotecan, and temozolomide with the addition of maintenance therapy with vinorelbine and cyclophosphamide. Secondary Objectives * To assess the relation between pharmacogenetic variation in CEP72 genotype and vinca alkaloid (vincristine; vinorelbine) disposition in children with rhabdomyosarcoma. * To assess the relation between the pharmacogenetic variation in drug metabolizing enzymes and drug transporters, and the pharmacokinetics of vinca alkaloids, liposomal irinotecan, and cyclophosphamide in children with rhabdomyosarcoma. * To assess the extent of inter-patient variability in the pharmacokinetics of vinca alkaloids, liposomal irinotecan, and cyclophosphamide in children with rhabdomyosarcoma, and explore possible associations between drug disposition and patient spec…

This description comes directly from the study's public registry record.

Talk to the study team

Alberto Pappo, MD  ·  (901) 595-2322  ·  alberto.pappo@stjude.org

Always discuss trial participation with your own doctor first.

Locations (3)

Stanford UniversityPalo Alto, California, United StatesRecruiting
St. Jude Children's Research HospitalMemphis, Tennessee, United StatesRecruiting
Cook Children's Medical CenterFort Worth, Texas, United StatesNot Yet Recruiting

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Source record: clinicaltrials.gov/study/NCT06023641