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Study identifier: NCT05734196 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency

Condition: Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency · Autosomal Recessive Hypophosphatemic Rickets · Generalized Arterial Calcification of Infancy  ·  Sponsor: Inozyme Pharma

PhasePhase 1
Planned participants16
Who can joinAll sexes, N/A to 1 Year
Healthy volunteersNo

About this study

The primary purpose of Study INZ701-104 (the ENERGY study) is to assess the safety and tolerability of INZ-701 in infants with ENPP1 Deficiency or with ABCC6 Deficiency.

This description comes directly from the study's public registry record.

Talk to the study team

Trial Specialist  ·  +1 800-983-4587  ·  medinfo@bmrn.com

Medical Director, MD  ·  +1 800-983-4587  ·  medinfo@bmrn.com

Always discuss trial participation with your own doctor first.

Locations (7)

Rady Children's HospitalSan Diego, California, United StatesRecruiting
Boston Children's HospitalBoston, Massachusetts, United StatesWithdrawn
Nationwide Children's HospitalColumbus, Ohio, United StatesRecruiting
The Children's Hospital of PhiladelphiaPhiladelphia, Pennsylvania, United StatesRecruiting
The University of UtahSalt Lake City, Utah, United StatesWithdrawn
Hospital Sant Joan de DéuBarcelona, SpainTerminated
Royal Manchester Children's HospitalManchester, United KingdomTerminated

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Source record: clinicaltrials.gov/study/NCT05734196