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Study identifier: NCT05465174 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

Tovorafenib for Treatment of Craniopharyngioma in Children and Young Adults

Condition: Craniopharyngioma, Child · Craniopharyngioma · Recurrent Craniopharyngioma  ·  Sponsor: Sabine Mueller, MD, PhD

PhasePhase 2
Planned participants57
Who can joinAll sexes, 1 Year to 39 Years
Healthy volunteersNo

About this study

The current study assesses the tolerability and efficacy of monotherapy with pan-RAF-kinase (Tovorafenib) inhibition for the treatment of children and young adults with craniopharyngioma.

This description comes directly from the study's public registry record.

Talk to the study team

PNOC Operations Office  ·  877-827-3222  ·  PNOC029@ucsf.edu

Always discuss trial participation with your own doctor first.

Locations (20)

University of Alabama at BirminghamBirmingham, Alabama, United StatesRecruiting
Rady Children's Hospital/University of California, San DiegoSan Diego, California, United StatesRecruiting
University of California, San FranciscoSan Francisco, California, United StatesRecruiting
University of FloridaGainesville, Florida, United StatesRecruiting
Ann & Robert H. Lurie Children's Hospital of ChicagoChicago, Illinois, United StatesRecruiting
Riley Hospital for Children at Indiana University HealthIndianapolis, Indiana, United StatesRecruiting
John Hopkins UniversityBaltimore, Maryland, United StatesRecruiting
Dana-Farber/Boston Children's Harvard Medical SchoolBoston, Massachusetts, United StatesRecruiting
University of MichiganAnn Arbor, Michigan, United StatesRecruiting
Children's MinnesotaMinneapolis, Minnesota, United StatesRecruiting
St. Louis Children's Hospital Washington UniversitySt Louis, Missouri, United StatesRecruiting
NYU Langone HealthNew York, New York, United StatesRecruiting

+ 8 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT05465174