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Study identifier: NCT05419492 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome

Condition: Dravet Syndrome  ·  Sponsor: Encoded Therapeutics

PhasePhase 1/Phase 2
Planned participants47
Who can joinAll sexes, 6 Months to 17 Years
Healthy volunteersNo

About this study

ENDEAVOR is a Phase 1/2, 2-part, multicenter study to evaluate the safety and efficacy of ETX101 in participants with SCN1A-positive Dravet syndrome aged ≥6 to \<36 months (Part 1A), aged ≥48 months to \<18 years (Part 1B), and aged ≥6 to \<48 months (Part 2). Part 1A follows an open-label, dose-escalation design, Part 1B follows an open-label design, and Part 2 is a randomized, double-blind, sham delayed-treatment control study.

This description comes directly from the study's public registry record.

Talk to the study team

Encoded Patient Advocacy  ·  +1 (650) 398-4301  ·  patientadvocacy@encoded.com

Always discuss trial participation with your own doctor first.

Locations (14)

UCSF Benioff Children's HospitalsSan Francisco, California, United StatesRecruiting
Colorado Children's HospitalAurora, Colorado, United StatesRecruiting
Nicklaus Children's HospitalMiami, Florida, United StatesRecruiting
Ann & Robert H. Lurie Children's Hospital of ChicagoChicago, Illinois, United StatesRecruiting
Boston Children's HospitalBoston, Massachusetts, United StatesNot Yet Recruiting
Mott Children's HospitalAnn Arbor, Michigan, United StatesRecruiting
Mayo ClinicRochester, Minnesota, United StatesRecruiting
Duke Children's Hospital & Health CenterDurham, North Carolina, United StatesNot Yet Recruiting
Nationwide Children's HospitalColumbus, Ohio, United StatesNot Yet Recruiting
Oregon Health and Science University (OSHU)Portland, Oregon, United StatesRecruiting
Cook Children's Medical CenterFort Worth, Texas, United StatesRecruiting
The Royal Children's HospitalMelbourne, AustraliaRecruiting

+ 2 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT05419492