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Study identifier: NCT05286788 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

MEKTOVI® for the Treatment of Pediatric Adamantinomatous Craniopharyngioma

Condition: Adamantinous Craniopharyngioma · Recurrent Adamantinomatous Craniopharyngioma  ·  Sponsor: Nationwide Children's Hospital

PhasePhase 2
Planned participants38
Who can joinAll sexes, 1 Year to 39 Years
Healthy volunteersNo

About this study

MEKTOVI (binimetinib) is an oral, highly selective reversible inhibitor of mitogen-activated extracellular signal regulated kinase 1 (MEK1) and MEK2. The biological activity of binimetinib that has been evaluated bith in vitro and in vivo in a wide variety of tumor types In this Phase II, the drug will be used to treat pediatric patients diagnosed with recurrent Adamantinomatous Craniopharyngioma including patients who have undergone surgery and/or radiation therapy.

This description comes directly from the study's public registry record.

Talk to the study team

Kelsey H Troyer, PhD  ·  16147223284  ·  kelsey.troyer@nationwidechildrens.org

Always discuss trial participation with your own doctor first.

Locations (10)

Children's Hospital ColoradoAurora, Colorado, United StatesRecruiting
Children's National Medical CenterWashington D.C., District of Columbia, United StatesRecruiting
Nicklaus Children's HospitalMiami, Florida, United StatesRecruiting
Cincinnati Children's Hospital Medical CenterCincinnati, Ohio, United StatesRecruiting
Nationwide Children's HospitalColumbus, Ohio, United StatesRecruiting
Sydney Children's HospitalRandwick, New South Wales, AustraliaRecruiting
Queensland Children's HospitalSouth Brisbane, Queensland, AustraliaRecruiting
Perth Children's HospitalPerth, Western Australia, AustraliaRecruiting
British Columbia Children's HospitalVancouver, British Columbia, CanadaRecruiting
CHU Sainte-JustineMontreal, Quebec, CanadaRecruiting

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Source record: clinicaltrials.gov/study/NCT05286788