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Study identifier: NCT05224778 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

Condition: Congenital Myotonic Dystrophy · CDM  ·  Sponsor: Virginia Commonwealth University

PhaseN/A
Planned participants50
Who can joinAll sexes, N/A to 59 Months
Healthy volunteersNo

About this study

The overall goal of the study is to establish valid clinical endpoint assessments for children with congenital myotonic dystrophy type 1 and develop biomarkers for the condition.

This description comes directly from the study's public registry record.

Talk to the study team

Ruby Langeslay  ·  804-828-8481  ·  ruby.langeslay@vcuhealth.org

Jennifer Raymond  ·  804-828-6318  ·  jennifer.raymond@vcuhealth.org

Always discuss trial participation with your own doctor first.

Locations (5)

University of California, Los AngelesLos Angeles, California, United StatesRecruiting
University of Kansas Medical CenterFairway, Kansas, United StatesRecruiting
University of Rochester Medical CenterRochester, New York, United StatesRecruiting
Virginia Commonwealth UniversityRichmond, Virginia, United StatesRecruiting
Centro Clinico NeMOMilan, ItalyRecruiting

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Source record: clinicaltrials.gov/study/NCT05224778