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Study identifier: NCT05005975 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

Extension Study to Evaluate Safety and Tolerability of Oral Dersimelagon (MT-7117) in Subjects With Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP)

Condition: EPP · XLP  ·  Sponsor: Tanabe Pharma America, Inc.

PhasePhase 3
Planned participants301
Who can joinAll sexes, 12 Years to 75 Years
Healthy volunteersNo

About this study

To evaluate the long-term safety and tolerability of oral dersimelagon.

This description comes directly from the study's public registry record.

Talk to the study team

Clinical Trials Information Desk, To prevent mis-communication,  ·  please e-mail  ·  information.US@mb.tanabe-pharma.com

Always discuss trial participation with your own doctor first.

Locations (51)

Marvel Clinical Research, LLCHuntington Beach, California, United StatesRecruiting
University of California at San Francisco - CSF Porphyria CenterSan Francisco, California, United StatesNot Yet Recruiting
University Of Miami School Of Medicine, Center For Liver DiseasesMiami, Florida, United StatesNot Yet Recruiting
Massachusetts General HospitalBoston, Massachusetts, United StatesNot Yet Recruiting
MetroBoston Clinical Partners, LLCBrighton, Massachusetts, United StatesRecruiting
Henry Ford Health SystemDetroit, Michigan, United StatesNot Yet Recruiting
Kansas City Research InstituteKansas City, Missouri, United StatesRecruiting
Icahn School of Medicine at Mount Sinai (ISSMS)-The Mount Sinai Hospital (MSH)New York, New York, United StatesRecruiting
Wake Forest University Baptist HealthWinston-Salem, North Carolina, United StatesRecruiting
Cleveland Clinic - Taussig Cancer InstituteCleveland, Ohio, United StatesNot Yet Recruiting
Remington-Davis Clinical ResearchColumbus, Ohio, United StatesRecruiting
Thomas Jefferson UniversityPhiladelphia, Pennsylvania, United StatesRecruiting

+ 39 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT05005975