Condition: Congenital Myotonic Dystrophy · Sponsor: AMO Pharma Limited
This is an open-label phase 2/3 study for individuals with Congenital Myotonic Dystrophy (Congenital DM1) who participated in the preceding AMO-02-MD-2-003 study or individuals with either Congenital or Childhood Onset DM1 who are treatment naïve.
This description comes directly from the study's public registry record.
Contact details are listed per location below or on the registry record.
Always discuss trial participation with your own doctor first.
| Arkansas Children's Hospital | Little Rock, Arkansas, United States | Recruiting |
| University of California, Los Angeles (UCLA) | Los Angeles, California, United States | Enrolling By Invitation |
| Stanford University | Palo Alto, California, United States | Enrolling By Invitation |
| Lurie's Children's Hospital | Chicago, Illinois, United States | Recruiting |
| University of Iowa Hospitals and Clinics | Iowa City, Iowa, United States | Recruiting |
| University of Rochester - Medical Center | Rochester, New York, United States | Recruiting |
| University of Pittsburgh Medical Center | Pittsburgh, Pennsylvania, United States | Recruiting |
| University of Utah Clinical Neurosciences Center | Salt Lake City, Utah, United States | Recruiting |
| Children's Hospital of The King's Daughters | Norfolk, Virginia, United States | Withdrawn |
| Virginia Commonwealth University-Department of Neurology - Muscular Dystrophy Translational Research Program | Richmond, Virginia, United States | Completed |
| The Bright Alliance | Randwick, New South Wales, Australia | Recruiting |
| Children's Hospital London Health Sciences Centre (LHSC) | London, Ontario, Canada | Enrolling By Invitation |
+ 2 more locations — full list on the registry record.
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Source record: clinicaltrials.gov/study/NCT05004129