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Study identifier: NCT04901936 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Condition: Paroxysmal Nocturnal Hemoglobinuria (PNH) · Paroxysmal Hemoglobinuria  ·  Sponsor: Apellis Pharmaceuticals, Inc.

PhasePhase 2
Planned participants12
Who can joinAll sexes, 12 Years to 17 Years
Healthy volunteersNo

About this study

The purpose of this study is to evaluate the safety, effectiveness, and biological activity (how the investigational medication is processed by the body) of pegcetacoplan in 12-17 year-olds (adolescents) who have paroxysmal nocturnal hemoglobinuria (PNH).

This description comes directly from the study's public registry record.

Talk to the study team

Apellis Clinical Trial Information Line  ·  1-833-284-6361 (833-CT Info-1)  ·  clinicaltrials@apellis.com

Always discuss trial participation with your own doctor first.

Locations (12)

Children's Hospital of AtlantaAtlanta, Georgia, United StatesRecruiting
Motol University HospitalPrague, CzechiaCompleted
Robert-Debré Hospital ParisParis, FranceNot Yet Recruiting
Hospital AmpangAmpang, MalaysiaRecruiting
Radboud University Hospital NijmegenNijmegen, NetherlandsCompleted
University Medical Center UtrechtUtrecht, NetherlandsRecruiting
University Children's HospitalBelgrade, SerbiaRecruiting
University Hospital Vall d'HebronBarcelona, SpainRecruiting
University Hospital 12 de OctubreMadrid, SpainRecruiting
Phramongkutklao Hospital and College of MedicineBangkok, ThailandCompleted
Maharaj Nakorn Chiang Mai hospitalChiang Mai, ThailandRecruiting
St. Mary's HospitalLondon, United KingdomCompleted

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Source record: clinicaltrials.gov/study/NCT04901936