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Study identifier: NCT04710576 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

A Study of Axatilimab at 3 Different Doses in Participants With Chronic Graft Versus Host Disease (cGVHD)

Condition: Chronic Graft-versus-host-disease  ·  Sponsor: Syndax Pharmaceuticals

PhasePhase 2
Planned participants296
Who can joinAll sexes, 2 Years to no upper limit
Healthy volunteersNo

About this study

This is a Phase 2 study to evaluate the efficacy, safety, and tolerability of axatilimab at 3 different dose levels in participants with recurrent or refractory active chronic graft versus host disease (cGVHD) who have received at least 2 prior lines of systemic therapy.

This description comes directly from the study's public registry record.

Talk to the study team

Syndax Pharmaceuticals  ·  781-419-1400  ·  clinicaltrials@syndax.com

Always discuss trial participation with your own doctor first.

Locations (121)

University of Alabama at Birmingham - Children's of AlabamaBirmingham, Alabama, United StatesCompleted
University of Alabama at BirminghamBirmingham, Alabama, United StatesRecruiting
City of HopeDuarte, California, United StatesActive Not Recruiting
University of Southern California Norris Comprehensive Cancer CenterLos Angeles, California, United StatesRecruiting
University of California, Los Angeles (UCLA) - Medical CenterLos Angeles, California, United StatesCompleted
Stanford Cancer CenterStanford, California, United StatesActive Not Recruiting
Children's National Medical CenterWashington D.C., District of Columbia, United StatesActive Not Recruiting
University of Florida (UF)Gainesville, Florida, United StatesCompleted
Mayo Clinic - JacksonvilleJacksonville, Florida, United StatesActive Not Recruiting
University of MiamiMiami, Florida, United StatesRecruiting
AdventHealth OrlandoOrlando, Florida, United StatesCompleted
MoffittTampa, Florida, United StatesActive Not Recruiting

+ 109 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT04710576