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Study identifier: NCT04626674 Synced from ClinicalTrials.gov · July 29, 2026
● Recruiting

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

Condition: Duchenne Muscular Dystrophy  ·  Sponsor: Sarepta Therapeutics, Inc.

PhasePhase 1
Planned participants83
Who can joinMale, 2 Years to no upper limit
Healthy volunteersNo

About this study

Cohort 8 (non-ambulatory participants) is currently enrolling new participants. Enrollment for Cohorts 1 through 7 has been completed. This is an open-label gene transfer therapy study evaluating the safety of and expression from delandistrogene moxeparvovec in participants with Duchenne Muscular Dystrophy (DMD). The maximum participant duration for this study is 156 weeks.

This description comes directly from the study's public registry record.

Talk to the study team

Sarepta Therapeutics Inc., For Clinical Trial Information, Select Option 4  ·  1-888-SAREPTA (1-888-727-3782)  ·  SareptAlly@Sarepta.com

Always discuss trial participation with your own doctor first.

Locations (7)

Arkansas Children's HospitalLittle Rock, Arkansas, United StatesRecruiting
Stanford UniversityPalo Alto, California, United StatesRecruiting
University of California, DavisSacramento, California, United StatesRecruiting
Washington University in St. LouisSt Louis, Missouri, United StatesRecruiting
Nationwide Children's HospitalColumbus, Ohio, United StatesActive Not Recruiting
Neurology Rare Disease CenterFlower Mound, Texas, United StatesRecruiting
Children's Hospital of The King's DaughtersNorfolk, Virginia, United StatesRecruiting

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Source record: clinicaltrials.gov/study/NCT04626674