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Study identifier: NCT04509050 Synced from ClinicalTrials.gov · July 28, 2026
● Recruiting

Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children

Condition: Cystic Fibrosis  ·  Sponsor: Sonya Heltshe

PhaseN/A
Planned participants210
Who can joinAll sexes, N/A to 10 Years
Healthy volunteersNo

About this study

This is a two-part, multi-center, prospective longitudinal, exploratory study of highly effective cystic fibrosis transmembrane conductance regulator (CFTR) modulators and their impact on children with cystic fibrosis (CF).

This description comes directly from the study's public registry record.

Talk to the study team

Rachael Buckingham  ·  206-884-7517  ·  rachael.buckingham@seattlechildrens.org

Anna Mead  ·  206-884-7531  ·  anna.mead@seattlechildrens.org

Always discuss trial participation with your own doctor first.

Locations (35)

The Children's Hospital Alabama, University of Alabama at BirminghamBirmingham, Alabama, United StatesRecruiting
Stanford University Medical CenterPalo Alto, California, United StatesRecruiting
Children's Hospital ColoradoAurora, Colorado, United StatesRecruiting
Nemours Children's ClinicJacksonville, Florida, United StatesRecruiting
University of MiamiMiami, Florida, United StatesRecruiting
The Nemours Children's Clinic - OrlandoOrlando, Florida, United StatesRecruiting
Riley Hospital for ChildrenIndianapolis, Indiana, United StatesRecruiting
University of IowaIowa City, Iowa, United StatesRecruiting
University of Kansas Medical CenterKansas City, Kansas, United StatesRecruiting
Boston Children's HospitalBoston, Massachusetts, United StatesRecruiting
University of Michigan, Michigan MedicineAnn Arbor, Michigan, United StatesRecruiting
Helen DeVos Children's HospitalGrand Rapids, Michigan, United StatesRecruiting

+ 23 more locations — full list on the registry record.

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Source record: clinicaltrials.gov/study/NCT04509050